Are we prepared to deliver gene-targeted therapies for rare diseases?

Timothy W. Yu, Stephen F. Kingsmore, Robert C. Green, Tippi MacKenzie, Melissa Wasserstein, Michele Caggana, Nina B. Gold, Annie Kennedy, Priya S. Kishnani, Matthew Might, Phillip J. Brooks, Jill A. Morris, Melissa A. Parisi, Tiina K. Urv

Research output: Contribution to journalComment/debatepeer-review

6 Scopus citations

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Medicine & Life Sciences