Efficacy and ototoxicity of different cyclodextrins in Niemann-Pick C disease

Cristin D. Davidson, Yonatan I. Fishman, István Puskás, Julianna Szemán, Tamás Sohajda, Leslie A. Mccauliff, Jakub Sikora, Judith Storch, Marie T. Vanier, Lajos Szente, Steven U. Walkley, Kostantin Dobrenis

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Medicine & Life Sciences